MDA TO PLAN NORTH AMERICAN CLINICAL
TRIALS NETWORK FOR MUSCULAR DYSTROPHY

TUCSON, Ariz., June 9, 2004 — Some 35 neuromuscular disease experts, along with biotechnology and government representatives, will meet Friday and Saturday at the Westin La Paloma here to develop a large-scale network to test potential treatments in muscular dystrophy, the Muscular Dystrophy Association (MDA) announced today.

The network, which could allow for centralized data collection and data sharing, is being developed in anticipation of an increased number of therapeutic trials for muscular dystrophy. Such a network could also be used to learn how to better manage medical complications of these diseases, including breathing and heart problems.

Initial emphasis will be on trials for Duchenne MD, a severe, childhood-onset form of the disease.

“MDA investigators are working hard to translate new findings in the lab into therapies that will benefit those served by MDA,” Director of Research Development Sharon Hesterlee said. “We want to make sure they have all the tools they need to accomplish these goals.”
Susan Iannaconne, a physician specializing in neuromuscular disease at the University of Texas Southwestern Medical Center at Dallas, and Richard Moxley, a physician specializing in neuromuscular disease at the University of Rochester (N.Y.) Medical Center, will co-chair the conference.

MDA is the nonprofit health agency dedicated to curing muscular dystrophy, ALS and related diseases by funding worldwide research. The Association also provides comprehensive health care and support services, advocacy and education.